Before the deaths of her children, Clancy got 30 prescriptions from five clinicians and two hospitals. Lack of coordination cited as key factor in tragic outcome.
Like Ultragenyx, Ionis and Oak Hill Bio are developing their own antisense treatments for Angelman syndrome.
Mass General Brigham's Medicare Advantage plan is dropping coverage of Dana-Farber, a top cancer center.
The pair of cases mark a milestone for the biotech company eGenesis in its wider effort to advance xenografts.
For children with schizophrenia, clozapine can be close to miraculous. Doctors are too reluctant to use it, writes expert.
Ionis Pharmaceuticals receives FDA approval for Zanvastro, the first disease-modifying therapy for rare and fatal neurological Alexander disease.
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