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top stories
1. Exclusive: Third death in China's popular but opaque trials revealed, this time in CAR-T
2. BioMarin does another small deal to get early-stage bone disease asset
3. Amylyx declares late-stage win with a GLP-1 antagonist in its post-ALS reset
4. Leo Pharma to license Tanabe’s rare disease drug for pain with sun exposure
5. Drugmakers voice support of US probe into Germany’s drug pricing plans
6. AstraZeneca touts separate late-stage lung cancer wins with Tagrisso, Enhertu
more stories
 
Karen Weintraub
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Ryan Cross reveals that a man in his 50s died earlier this year in a Chinese investigator-initiated trial, marking the third such death reported in recent weeks. Read on for details.

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Karen Weintraub
Deputy Editor, Endpoints News
1
by Ryan Cross

A pa­tient with an au­toim­mune dis­ease has died af­ter re­ceiv­ing an ex­per­i­men­tal ge­net­ic med­i­cine from a biotech start­up in Chi­na, End­points News has learned.

The...

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2
by Kyle LaHucik

A week af­ter end­ing de­vel­op­mentof a rare dis­ease drug from a $270 mil­lion ac­qui­si­tion, Bio­Marin is back at the deal­mak­ing ta­ble for a very...

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Amylyx co-CEOs Justin Klee (L) and Joshua Cohen
3
by Max Gelman

Af­ter a tur­bu­lent few years re­search­ing ALS, Amy­lyx Phar­ma­ceu­ti­cals said it has notched a suc­cess in its at­tempt to re­build as a GLP-1 biotech.

A...

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Christophe Bourdon, Leo Pharma CEO
4
by Ayisha Sharma

Leo Phar­ma said it will pay Japan’s Tan­abe Phar­ma up to $435 mil­lion in up­front and near-term pay­ments to li­cense an oral drug for a...

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